News Featured Promising News from a Clinical Study in Becker Muscular Dystrophy Latest News in Sickle Cell Disease Perceptions of Pain: Research Shows It’s Personal Why Men's Health Week Matters for the Rare Community Mark Your Calendar for TSF's Atlanta Patient Day May Is Myositis Awareness Month Why 2024 Is Already an Encouraging Year for the Rare Disease Community National Tay-Sachs & Allied Diseases Association Hosts First of Its Kind Drug Development Meeting for GM2 Edgewise Therapeutics: New Treatments for Duchenne and Becker Muscular Dystrophy From Medical Advisor to Fundraiser: A Mom and Know Rare Team Member Helps the Hospital that Helped Her Clinical Trial Paves the Way for a Groundbreaking New Myasthenia Gravis Treatment Understanding COVID-19 and Myositis: Key Insights into Muscle Inflammation and Pain A personal approach to the development of new treatments in rare disease New Way to Study the Mental Capabilities of Children Over 12 With PA or MMA Famously Rare: Celebrities Diagnosed With Rare Diseases DNA Today Podcast: Propionic and Methylmalonic Acidemia with HemoShear Therapeutics Research in Action: Measuring Patient-Reported Outcomes in FSGS A Rare Disease True Crime Story Effects of a 6-Month Yoga Program on Kidney Function and Quality of Life DNA Today Podcast: Mitochondrial Disorders with Alejandro Dorenbaum Confronting Racial and Ethnic Disparities in Rare Disease Care One Bad Take: A Daily Newspaper Misses the Target on Prenatal Testing Primary Mitochondrial Myopathies: Researchers Explore New Pathways for Treatment Rare Disease Diversity Coalition Formed To End Racial Disparities In Rare Disease Diagnosis, Research, And Treatment Women Who Broke Barriers in Rare Disease Fusion Oncogene: When Two Genes Come Together, They May Cause Tumors to Grow Rare Cancer Research: Leading the Way to the Development of New Cancer Therapies Advancements in Rare Disease Treatment: Progress and Future Outlook
